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CLINICAL_TRIALS research · 2025-12-17

Clinical Trial Update: Long-term Safety and Efficacy Study of Fitusiran in Patients With Hemophilia A or B, With or Without Inhibitory Antibodies to Factor VIII or IX [Phase 3]

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Summary

An update on the ongoing Phase 3 long-term safety and efficacy study of fitusiran in patients with Hemophilia A or B, including those with inhibitors to factor …

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Diseases / indications

Drugs mentioned

  • Fitusiran (fitusiran)

Snippet

Sponsor: Genzyme, a Sanofi Company | Conditions: Hemophilia | Phase 3 | Status: ACTIVE_NOT_RECRUITING