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CLINICAL_TRIALS withdrawal · 2025-12-18

Clinical Trial Update: Safety, Tolerability and Effect of ARC-AAT Injection on Circulating and Intrahepatic Alpha-1 Antitrypsin Levels [Phase 2]

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Summary

Phase 2 study ARC-AAT for Alpha-1 Antitrypsin Deficiency was withdrawn; the trial evaluated safety, tolerability, and effects on circulating and intrahepatic al…

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Diseases / indications

Drugs mentioned

  • ARC-AAT

Snippet

Sponsor: Arrowhead Pharmaceuticals | Conditions: Alpha-1 Antitrypsin Deficiency | Phase 2 | Status: WITHDRAWN