Catalyst Wire Dossier Catalyst Wire Dossier
CLINICAL_TRIALS research · 2025-12-18

Clinical Trial Update: An Observational LTFU Study for Patients Previously Treated With Autologous ex Vivo Gene Therapy for ADA-SCID

View source ↗

Summary

This clinical trial update describes an observational follow-up study of patients previously treated with autologous ex vivo gene therapy for ADA-SCID, currentl…

Upgrade for the full analysis, importance score, and drug timeline.

Diseases / indications

Snippet

Sponsor: University of California, Los Angeles | Conditions: Adenosine Deaminase Deficiency, Severe Combined Immunodeficiency (SCID) | Status: ENROLLING_BY_INVITATION