CLINICAL_TRIALS
research
· 2025-12-18
Clinical Trial Update: An Observational LTFU Study for Patients Previously Treated With Autologous ex Vivo Gene Therapy for ADA-SCID
Summary
This clinical trial update describes an observational follow-up study of patients previously treated with autologous ex vivo gene therapy for ADA-SCID, currentl…
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Diseases / indications
Snippet
Sponsor: University of California, Los Angeles | Conditions: Adenosine Deaminase Deficiency, Severe Combined Immunodeficiency (SCID) | Status: ENROLLING_BY_INVITATION