Clinical Trial Update: A Study to Investigate the Efficacy and Safety of OTL-203 in Subjects With MPS-IH Compared With Standard of Care With Allogeneic HSCT [Phase 3]

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Summary

This update covers a Phase 3 clinical trial evaluating OTL-203 for MPS-IH (Hurler syndrome) compared with standard of care using allogeneic hematopoietic stem c…

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Diseases / indications

• Mucopolysaccharidosis Type Hurler Syndrome

Drugs mentioned

• OTL-203

Snippet

Sponsor: Orchard Therapeutics | Conditions: MPS-IH (Hurler Syndrome) | Phase 3 | Status: ACTIVE_NOT_RECRUITING