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CLINICAL_TRIALS research · 2025-12-23

Clinical Trial Update: Wolfram Syndrome and WFS1-related Disorders International Registry and Clinical Study

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Summary

This update describes an international registry and clinical study for Wolfram syndrome and WFS1-related disorders, which is currently recruiting participants.

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Diseases / indications

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Sponsor: Washington University School of Medicine | Conditions: Wolfram Syndrome, Diabetes Mellitus | Status: RECRUITING