CLINICAL_TRIALS
trial_result
· 2025-12-23
Clinical Trial Update: Study of Danicopan as Add-on Treatment to Ravulizumab or Eculizumab in Pediatric Participants With PNH Who Have Clinically Significant Extravascular Hemolysis [Phase 3]
Summary
Phase 3 clinical trial update indicates danicopan as an add-on to ravulizumab or eculizumab in pediatric patients with paroxysmal nocturnal hemoglobinuria and c…
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Diseases / indications
Drugs mentioned
Snippet
Sponsor: Alexion Pharmaceuticals, Inc. | Conditions: Paroxysmal Nocturnal Hemoglobinuria, PNH | Phase 3 | Status: RECRUITING