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CLINICAL_TRIALS trial_result · 2025-12-23

Clinical Trial Update: Study of Danicopan as Add-on Treatment to Ravulizumab or Eculizumab in Pediatric Participants With PNH Who Have Clinically Significant Extravascular Hemolysis [Phase 3]

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Summary

Phase 3 clinical trial update indicates danicopan as an add-on to ravulizumab or eculizumab in pediatric patients with paroxysmal nocturnal hemoglobinuria and c…

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Diseases / indications

Drugs mentioned

  • Danicopan (danicopan)
  • Eculizumab (eculizumab)
  • Ravulizumab (ravulizumab)

Snippet

Sponsor: Alexion Pharmaceuticals, Inc. | Conditions: Paroxysmal Nocturnal Hemoglobinuria, PNH | Phase 3 | Status: RECRUITING