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CLINICAL_TRIALS withdrawal · 2025-12-23

Clinical Trial Update: A Non-interventional, Post-Marketing Study to Describe Outcome of Nitisinone Treatment in HT-1 Patients

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Summary

A non-interventional post-marketing study assessing outcomes of nitisinone treatment in patients with hereditary tyrosinemia type I, which has been withdrawn.

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Diseases / indications

Drugs mentioned

  • Orfadin (nitisinone)

Snippet

Sponsor: Swedish Orphan Biovitrum | Conditions: Hereditary Tyrosinemia, Type I | Status: WITHDRAWN