CLINICAL_TRIALS
withdrawal
· 2025-12-23
Clinical Trial Update: A Non-interventional, Post-Marketing Study to Describe Outcome of Nitisinone Treatment in HT-1 Patients
Summary
A non-interventional post-marketing study assessing outcomes of nitisinone treatment in patients with hereditary tyrosinemia type I, which has been withdrawn.
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Diseases / indications
Drugs mentioned
Snippet
Sponsor: Swedish Orphan Biovitrum | Conditions: Hereditary Tyrosinemia, Type I | Status: WITHDRAWN