Clinical Trial Update: Observational Study of Neurofilament Light Chain (NfL) as a Biomarker in Asymptomatic Carriers of the Transthyretin (TTR) Variants and Patients With Hereditary Transthyretin-mediated (hATTR) Amyloidosis With Polyneuropathy

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Summary

An observational study is evaluating neurofilament light chain as a biomarker in asymptomatic carriers of transthyretin variants and in patients with hereditary…

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Diseases / indications

• Hereditary Transthyretin-mediated Amyloidosis
• Hereditary Transthyretin-mediated Amyloidosis with Polyneuropathy

Snippet

Sponsor: Alnylam Pharmaceuticals | Conditions: Hereditary Amyloidosis, Transthyretin-Related, Asymptomatic Carrier State | Status: RECRUITING