Clinical Trial Update: Short and Long Term Treatment With 4-AP in Ambulatory SMA Patients [Phase 2, Phase 3]

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Summary

Phase 2 and Phase 3 clinical trials evaluated short-term and long-term treatment with 4-aminopyridine (4-AP) in ambulatory patients with spinal muscular atrophy…

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Diseases / indications

• Spinal Muscular Atrophy

Drugs mentioned

• 4-aminopyridine (4-aminopyridine)

Snippet

Sponsor: Columbia University | Conditions: Spinal Muscular Atrophy | Phase 2, Phase 3 | Status: COMPLETED | Results posted: 2024-09-03