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CLINICAL_TRIALS trial_result · 2026-01-07

Clinical Trial Update: Long-term Extension of GTX-102 in Angelman Syndrome [Phase 3]

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Summary

This notice reports a long-term extension study for GTX-102 in Angelman Syndrome, a Phase 3 trial that is currently enrolling by invitation.

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Diseases / indications

Drugs mentioned

  • GTX-102

Snippet

Sponsor: Ultragenyx Pharmaceutical Inc | Conditions: Angelman Syndrome | Phase 3 | Status: ENROLLING_BY_INVITATION