Clinical Trial Update: Rare Glycogen Storage Diseases Natural History Study

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Summary

Duke University is conducting a natural history study of rare glycogen storage diseases and is currently recruiting participants to collect longitudinal data ac…

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Diseases / indications

• Danon Disease
• Glycogen Storage Disease Type 0a
• Glycogen Storage Disease Type 0b
• Glycogen Storage Disease Type Vii
• Polyglucosan Body Myopathy Type
• Prkag2 Deficiency
• Rbck1 Deficiency

Snippet

Sponsor: Duke University | Conditions: Glycogen Storage Disease, GSD Type 0A | Status: RECRUITING