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CLINICAL_TRIALS trial_result · 2026-01-08

Clinical Trial Update: Study of Safety and Efficacy of Genome-edited Hematopoietic Stem and Progenitor Cells in Sickle Cell Disease (SCD) [Phase 1]

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Summary

A Phase 1 study of genome-edited hematopoietic stem and progenitor cell therapy for sickle cell disease has been terminated.

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Diseases / indications

Drugs mentioned

  • Genome-edited hematopoietic stem and progenitor cell therapy

Snippet

Sponsor: Novartis Pharmaceuticals | Conditions: Sickle Cell Disease | Phase 1 | Status: TERMINATED