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CLINICAL_TRIALS trial_result · 2026-01-13

Clinical Trial Update: A Study of Avapritinib in Pediatric Patients With Solid Tumors Dependent on KIT or PDGFRA Signaling [Phase 1, Phase 2]

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Summary

This pediatric Phase 1/2 trial of avapritinib in KIT- or PDGFRA-dependent solid tumors and central nervous system tumors has completed.

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Diseases / indications

Drugs mentioned

  • AYVAKIT (avapritinib)

Snippet

Sponsor: Blueprint Medicines Corporation | Conditions: Solid Tumor, Unspecified, Child, Relapsed Solid Neoplasm | Phase 1, Phase 2 | Status: COMPLETED