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CLINICAL_TRIALS research · 2026-01-13

Clinical Trial Update: Natural History Study of Patients With Succinic Semialdehyde Dehydrogenase (SSADH) Deficiency

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Summary

An observational natural history study recruiting patients with succinic semialdehyde dehydrogenase deficiency to characterize disease progression.

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Diseases / indications

Snippet

Sponsor: Boston Children's Hospital | Conditions: Succinic Semialdehyde Dehydrogenase Deficiency | Status: RECRUITING