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CLINICAL_TRIALS research · 2026-01-14

Clinical Trial Update: Cerliponase Alfa Observational Study in the US

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Summary

An update on an observational US study of cerliponase alfa for late-infantile neuronal ceroid lipofuscinosis type 2, noting the study is active but not recruiti…

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Diseases / indications

Drugs mentioned

  • BRINEURA (cerliponase alfa)

Snippet

Sponsor: BioMarin Pharmaceutical | Conditions: Late-Infantile Neuronal Ceroid Lipofuscinosis Type 2 | Status: ACTIVE_NOT_RECRUITING