CLINICAL_TRIALS
research
· 2026-01-14
Clinical Trial Update: Cerliponase Alfa Observational Study in the US
Summary
An update on an observational US study of cerliponase alfa for late-infantile neuronal ceroid lipofuscinosis type 2, noting the study is active but not recruiti…
Upgrade for the full analysis, importance score, and drug timeline.
Diseases / indications
Drugs mentioned
Snippet
Sponsor: BioMarin Pharmaceutical | Conditions: Late-Infantile Neuronal Ceroid Lipofuscinosis Type 2 | Status: ACTIVE_NOT_RECRUITING