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CLINICAL_TRIALS research · 2024-09-19

Clinical Trial Update: Leber Congenital Amaurosis Inherited Blindness of Gene Therapy Trial(LIGHT) [EARLY_Phase 1]

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Summary

Early phase 1 clinical trial update (LIGHT) investigates a gene therapy for Leber congenital amaurosis, conducted by Xinhua Hospital and Shanghai Jiao Tong Univ…

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Diseases / indications

Drugs mentioned

  • LIGHT gene therapy (investigational)

Snippet

Sponsor: Xinhua Hospital, Shanghai Jiao Tong University School of Medicine | Conditions: Leber Congenital Amaurosis | EARLY_Phase 1 | Status: ACTIVE_NOT_RECRUITING