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CLINICAL_TRIALS research · 2026-01-23

Clinical Trial Update: Tianasen (ASO-GNAO1) for GNAO1-Encephalopathy With Epilepsy and Movement Disorders. [Phase 1, Phase 2]

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Summary

Phase 1/2 clinical trial evaluating Tianasen (ASO-GNAO1) for GNAO1-related encephalopathy presenting with epilepsy and movement disorders; currently recruiting.

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Diseases / indications

Drugs mentioned

  • Tianasen (ASO-GNAO1)

Snippet

Sponsor: Pirogov Russian National Research Medical University | Conditions: GNAO1, Epilepsy | Phase 1, Phase 2 | Status: RECRUITING