CLINICAL_TRIALS
research
· 2026-01-28
Clinical Trial Update: Treatment of TK2 Deficiency With Thymidine and Deoxycytidine [Phase 1, Phase 2]
Summary
This clinical trial entry reports a Phase 1/2 study evaluating thymidine and deoxycytidine for TK2 deficiency. The trial is currently active and not recruiting.
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Diseases / indications
Drugs mentioned
Snippet
Sponsor: Columbia University | Conditions: Mitochondrial DNA Depletion Syndrome 2 Myopathic Type, Thymidine Kinase 2 Deficiency | Phase 1, Phase 2 | Status: ACTIVE_NOT_RECRUITING