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CLINICAL_TRIALS trial_result · 2024-09-19

Clinical Trial Update: Study to Evaluate Safety, Tolerability, PK and PD of DCR-PHXC in PH Type 3 Patients [Phase 1]

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Summary

A Phase 1 study evaluating safety, tolerability, pharmacokinetics and pharmacodynamics of DCR-PHXC in Primary Hyperoxaluria Type 3 has completed.

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Diseases / indications

Drugs mentioned

  • DCR-PHXC

Snippet

Sponsor: Dicerna Pharmaceuticals, Inc., a Novo Nordisk company | Conditions: Primary Hyperoxaluria Type 3 | Phase 1 | Status: COMPLETED