Catalyst Wire Dossier Catalyst Wire Dossier
CLINICAL_TRIALS research · 2026-02-02

Clinical Trial Update: Gene Transfer Study in Patients With Late Onset Pompe Disease [Phase 1, Phase 2]

View source ↗

Summary

This clinical trial update describes an ongoing phase 1/2 gene transfer study for late-onset Pompe disease sponsored by Astellas Gene Therapies.

Upgrade for the full analysis, importance score, and drug timeline.

Diseases / indications

Drugs mentioned

  • Gene therapy product for Pompe disease

Snippet

Sponsor: Astellas Gene Therapies | Conditions: Pompe Disease (Late-onset) | Phase 1, Phase 2 | Status: ACTIVE_NOT_RECRUITING