CLINICAL_TRIALS
research
· 2026-02-02
Clinical Trial Update: Gene Transfer Study in Patients With Late Onset Pompe Disease [Phase 1, Phase 2]
Summary
This clinical trial update describes an ongoing phase 1/2 gene transfer study for late-onset Pompe disease sponsored by Astellas Gene Therapies.
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Diseases / indications
Drugs mentioned
Snippet
Sponsor: Astellas Gene Therapies | Conditions: Pompe Disease (Late-onset) | Phase 1, Phase 2 | Status: ACTIVE_NOT_RECRUITING