Clinical Trial Update: Long-term Follow-up Study of Patients Who Received hLB-001 Gene Therapy

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Summary

Long-term follow-up data from patients who received the hLB-001 gene therapy for Methylmalonic Acidemia is being collected, with the study currently active but …

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Diseases / indications

• Methylmalonic Acidemia

Drugs mentioned

• hLB-001

Snippet

Sponsor: Alexion Pharmaceuticals, Inc. | Conditions: Methylmalonic Acidemia | Status: ACTIVE_NOT_RECRUITING