CLINICAL_TRIALS
research
· 2026-02-09
Clinical Trial Update: JAG201 Gene Therapy Study in Children & Adults With SHANK3 Haploinsufficiency [Phase 1, Phase 2]
Summary
Phase 1/2 clinical trial of JAG201 Gene Therapy for SHANK3 haploinsufficiency and Phelan-McDermid syndrome, currently recruiting.
Upgrade for the full analysis, importance score, and drug timeline.
Diseases / indications
Drugs mentioned
Snippet
Sponsor: Jaguar Gene Therapy, LLC | Conditions: SHANK3 Haploinsufficiency, Phelan-McDermid Syndrome | Phase 1, Phase 2 | Status: RECRUITING