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CLINICAL_TRIALS research · 2026-02-09

Clinical Trial Update: JAG201 Gene Therapy Study in Children & Adults With SHANK3 Haploinsufficiency [Phase 1, Phase 2]

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Summary

Phase 1/2 clinical trial of JAG201 Gene Therapy for SHANK3 haploinsufficiency and Phelan-McDermid syndrome, currently recruiting.

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Diseases / indications

Drugs mentioned

  • JAG201 Gene Therapy

Snippet

Sponsor: Jaguar Gene Therapy, LLC | Conditions: SHANK3 Haploinsufficiency, Phelan-McDermid Syndrome | Phase 1, Phase 2 | Status: RECRUITING