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CLINICAL_TRIALS trial_result · 2026-02-10

Clinical Trial Update: A Safety and Efficacy Study Evaluating CS-101 in Subjects With β-Thalassemia Major [Phase 1]

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Summary

Phase 1 safety and efficacy study of CS-101 in beta-thalassemia major has completed.

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Diseases / indications

Drugs mentioned

  • CS-101

Snippet

Sponsor: CorrectSequence Therapeutics Co., Ltd | Conditions: Beta-Thalassemia Major | Phase 1 | Status: COMPLETED