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CLINICAL_TRIALS research · 2026-02-11

Clinical Trial Update: GammaGA: Prevalence of Acid Sphingomyelinase Deficiency Disease (ASMD) and Gaucher Disease in Patients With Monoclonal Gammopathies and/or Multiple Myeloma

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Summary

Clinical trial update for GammaGA examining how common acid sphingomyelinase deficiency (ASMD) and Gaucher disease are in patients with monoclonal gammopathies …

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Diseases / indications

Drugs mentioned

  • GammaGA

Snippet

Sponsor: Fundación Española de Hematología y Hemoterapía | Conditions: Gaucher Disease, Acid SphingoMyelinase Deficiency | Status: RECRUITING