CLINICAL_TRIALS
research
· 2026-02-11
Clinical Trial Update: GammaGA: Prevalence of Acid Sphingomyelinase Deficiency Disease (ASMD) and Gaucher Disease in Patients With Monoclonal Gammopathies and/or Multiple Myeloma
Summary
Clinical trial update for GammaGA examining how common acid sphingomyelinase deficiency (ASMD) and Gaucher disease are in patients with monoclonal gammopathies …
Upgrade for the full analysis, importance score, and drug timeline.
Diseases / indications
Drugs mentioned
Snippet
Sponsor: Fundación Española de Hematología y Hemoterapía | Conditions: Gaucher Disease, Acid SphingoMyelinase Deficiency | Status: RECRUITING