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CLINICAL_TRIALS research · 2026-02-13

Clinical Trial Update: Autologous Gene Therapy for Artemis-Deficient SCID [Phase 1, Phase 2]

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Summary

Clinical trial update for autologous Artemis-deficient SCID gene therapy, currently recruiting in Phase 1/Phase 2.

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Diseases / indications

Drugs mentioned

  • Autologous Artemis-deficient SCID gene therapy

Snippet

Sponsor: University of California, San Francisco | Conditions: Severe Combined Immunodeficiency | Phase 1, Phase 2 | Status: RECRUITING