CLINICAL_TRIALS
research
· 2026-02-13
Clinical Trial Update: Autologous Gene Therapy for Artemis-Deficient SCID [Phase 1, Phase 2]
Summary
Clinical trial update for autologous Artemis-deficient SCID gene therapy, currently recruiting in Phase 1/Phase 2.
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Diseases / indications
Drugs mentioned
Snippet
Sponsor: University of California, San Francisco | Conditions: Severe Combined Immunodeficiency | Phase 1, Phase 2 | Status: RECRUITING