CLINICAL_TRIALS
research
· 2026-02-17
Clinical Trial Update: Clinical Study of DTX301 AAV-Mediated Gene Transfer for Ornithine Transcarbamylase (OTC) Deficiency [Phase 3]
Summary
Clinical trial update indicating that Ultragenyx's DTX301 AAV-mediated gene transfer for ornithine transcarbamylase deficiency is a Phase 3 study and currently …
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Drugs mentioned
Snippet
Sponsor: Ultragenyx Pharmaceutical Inc | Conditions: OTC Deficiency | Phase 3 | Status: ACTIVE_NOT_RECRUITING