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CLINICAL_TRIALS research · 2026-02-17

Clinical Trial Update: Clinical Study of DTX301 AAV-Mediated Gene Transfer for Ornithine Transcarbamylase (OTC) Deficiency [Phase 3]

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Summary

Clinical trial update indicating that Ultragenyx's DTX301 AAV-mediated gene transfer for ornithine transcarbamylase deficiency is a Phase 3 study and currently …

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Diseases / indications

Drugs mentioned

  • DTX301

Snippet

Sponsor: Ultragenyx Pharmaceutical Inc | Conditions: OTC Deficiency | Phase 3 | Status: ACTIVE_NOT_RECRUITING