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CLINICAL_TRIALS research · 2026-02-17

Clinical Trial Update: Assess Long-Term Safety of Danicopan Add-on Therapy in Participants With Paroxysmal Nocturnal Hemoglobinuria: Analysis of IPIG-Registry Data

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Summary

Clinical trial update analyzing long-term safety of Danicopan as add-on therapy in paroxysmal nocturnal hemoglobinuria using IPIG-Registry data.

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Diseases / indications

Drugs mentioned

  • Danicopan (danicopan)

Snippet

Sponsor: Alexion Pharmaceuticals, Inc. | Conditions: Paroxysmal Nocturnal Hemoglobinuria, PNH | Status: ACTIVE_NOT_RECRUITING