CLINICAL_TRIALS
trial_result
· 2026-02-19
Clinical Trial Update: Long Term Follow Up to Evaluate DTX301 in Adults With Late-Onset OTC Deficiency
Summary
Clinical trial update providing long-term follow-up data for DTX301 in adults with late-onset Ornithine Transcarbamylase deficiency. The study is currently acti…
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Diseases / indications
Drugs mentioned
Snippet
Sponsor: Ultragenyx Pharmaceutical Inc | Conditions: Ornithine Transcarbamylase (OTC) Deficiency | Status: ACTIVE_NOT_RECRUITING