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CLINICAL_TRIALS trial_result · 2026-02-19

Clinical Trial Update: Long Term Follow Up to Evaluate DTX301 in Adults With Late-Onset OTC Deficiency

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Summary

Clinical trial update providing long-term follow-up data for DTX301 in adults with late-onset Ornithine Transcarbamylase deficiency. The study is currently acti…

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Diseases / indications

Drugs mentioned

  • DTX301

Snippet

Sponsor: Ultragenyx Pharmaceutical Inc | Conditions: Ornithine Transcarbamylase (OTC) Deficiency | Status: ACTIVE_NOT_RECRUITING