Clinical Trial Update: Phase 1/2 Study of MZ-1866, an AAV-9 Gene Therapy Delivered by Intracerebroventricular Injection to Participants With Pitt Hopkins Syndrome [Phase 1, Phase 2]

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Summary

This is an update on an early-phase clinical trial of MZ-1866, an AAV-9 gene therapy delivered by intracerebroventricular injection for Pitt-Hopkins syndrome, c…

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Diseases / indications

• Pitt Hopkins Syndrome

Drugs mentioned

• MZ-1866

Snippet

Sponsor: Mahzi Therapeutics | Conditions: Pitt Hopkins Syndrome | Phase 1, Phase 2 | Status: RECRUITING