Clinical Trial Update: A Prospective Study of Pediatric Participants up to 16 Years of Age With Methylmalonic Acidemia (MMA) Due to Mutations in the MMUT Gene

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Summary

This clinical trial update describes a prospective study enrolling pediatric participants up to 16 years with methylmalonic acidemia due to MMUT gene mutations.…

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Diseases / indications

• Methylmalonic Acidemia

Snippet

Sponsor: Genespire Srl | Conditions: Methylmalonic Acidemia (MMA) | Status: NOT_YET_RECRUITING