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CLINICAL_TRIALS trial_result · 2026-03-02

Clinical Trial Update: Safety Evaluation of Gene Therapy in Leber Hereditary Optic Neuropathy (LHON) Patients [Phase 1, Phase 2]

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Summary

A safety evaluation update from a Phase 1/2 gene therapy trial in Leber hereditary optic neuropathy, reporting safety outcomes without efficacy claims.

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Diseases / indications

Drugs mentioned

  • LUMEVOI (lenadogene nolparvovec)

Snippet

Sponsor: GenSight Biologics | Conditions: Leber Hereditary Optic Neuropathy | Phase 1, Phase 2 | Status: COMPLETED