Clinical Trial Update: Intracerebral Gene Therapy for Children With Early Onset Forms of Metachromatic Leukodystrophy [Phase 1, Phase 2]

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Summary

This clinical trial update reports the completion of Phase 1/2 testing of an intracerebral gene therapy for children with early-onset Metachromatic Leukodystrop…

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Diseases / indications

• Metachromatic Leukodystrophy

Snippet

Sponsor: Institut National de la Santé Et de la Recherche Médicale, France | Conditions: Metachromatic Leukodystrophy | Phase 1, Phase 2 | Status: COMPLETED