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CLINICAL_TRIALS research · 2026-03-02

Clinical Trial Update: A Natural History of Late Onset Tay-Sachs Disease

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Summary

A completed natural history study of GM2 gangliosidosis, including late-onset Tay-Sachs disease, sponsored by Massachusetts General Hospital.

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Diseases / indications

Snippet

Sponsor: Massachusetts General Hospital | Conditions: GM2 Gangliosidosis | Status: COMPLETED