Clinical Trial Update: A One Visit Follow Up of Adults With Fabry Disease Who Started Long-term Enzyme Replacement Therapy As Children [NA]

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Summary

A completed follow-up study in adults with Fabry disease who began enzyme replacement therapy in childhood to assess long-term outcomes.

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Diseases / indications

• Fabry Disease

Drugs mentioned

• Enzyme replacement therapy (ERT) for Fabry disease

Snippet

Sponsor: Baylor Research Institute | Conditions: Quality of Life, Renal Insufficiency | NA | Status: COMPLETED