Clinical Trial Update: Translational Potential of ex Vivo Gene Therapy in GM2 Gangliosidosis

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Summary

A translational update on ex vivo gene therapy approaches for GM2 gangliosidosis (Tay-Sachs and Sandhoff diseases) with status not yet recruiting.

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Diseases / indications

• Sandhoff Disease
• Tay-sachs Disease

Snippet

Sponsor: Assistance Publique - Hôpitaux de Paris | Conditions: Tay-Sachs Disease Ganglioside, Sandhoff Disease Ganglioside | Status: NOT_YET_RECRUITING