CLINICAL_TRIALS
research
· 2026-03-06
Clinical Trial Update: Danicopan Early Access Program
Summary
An early access program for danicopan is described for patients with paroxysmal nocturnal hemoglobinuria (PNH), including those with extravascular hemolysis.
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Diseases / indications
Drugs mentioned
Snippet
Sponsor: Alexion Pharmaceuticals, Inc. | Conditions: Paroxysmal Nocturnal Hemoglobinuria, PNH | Status: AVAILABLE