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CLINICAL_TRIALS research · 2026-03-06

Clinical Trial Update: Danicopan Early Access Program

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Summary

An early access program for danicopan is described for patients with paroxysmal nocturnal hemoglobinuria (PNH), including those with extravascular hemolysis.

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Diseases / indications

Drugs mentioned

  • Danicopan (danicopan)

Snippet

Sponsor: Alexion Pharmaceuticals, Inc. | Conditions: Paroxysmal Nocturnal Hemoglobinuria, PNH | Status: AVAILABLE