Clinical Trial Update: Lysosomal Acid Lipase (LAL) Deficiency Registry

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Summary

Clinical trial registry update describing a Lysosomal Acid Lipase (LAL) deficiency registry that is currently recruiting to collect data on patients with LAL de…

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Diseases / indications

• Cholesterol Ester Storage Disease
• Lysosomal Acid Lipase Deficiency
• Wolman Disease

Drugs mentioned

• KANUMA (Sebelipase alfa)

Snippet

Sponsor: Alexion Pharmaceuticals, Inc. | Conditions: Lysosomal Acid Lipase Deficiency, Cholesterol Ester Storage Disease | Status: RECRUITING