CLINICAL_TRIALS
research
· 2026-03-10
Clinical Trial Update: A Global Prospective Observational Registry of Patients With Pompe Disease
Summary
Amicus Therapeutics is conducting a global prospective observational registry of patients with Pompe disease, currently recruiting.
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Diseases / indications
Snippet
Sponsor: Amicus Therapeutics | Conditions: Pompe Disease | Status: RECRUITING