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CLINICAL_TRIALS research · 2026-03-10

Clinical Trial Update: A Global Prospective Observational Registry of Patients With Pompe Disease

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Summary

Amicus Therapeutics is conducting a global prospective observational registry of patients with Pompe disease, currently recruiting.

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Diseases / indications

Snippet

Sponsor: Amicus Therapeutics | Conditions: Pompe Disease | Status: RECRUITING