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CLINICAL_TRIALS trial_result · 2026-03-10

Clinical Trial Update: Validation of Respiratory Epithelial Functional Assessment to Predict Clinical Efficacy of Orkambi®. [NA]

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Summary

A completed clinical trial update validating a respiratory epithelial functional assay to predict the clinical efficacy of Orkambi in people with cystic fibrosi…

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Diseases / indications

Drugs mentioned

  • ORKAMBI (lumacaftor and ivacaftor)

Snippet

Sponsor: Assistance Publique - Hôpitaux de Paris | Conditions: Cystic Fibrosis, Homozygous F508del Mutation | NA | Status: COMPLETED