Clinical Trial Update: A Natural History Study in Participants With Congenital Myasthenic Syndromes (CMS) Due to Mutations in DOK7, MUSK, AGRN, or LRP4

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Summary

A natural history study in participants with congenital myasthenic syndromes caused by mutations in DOK7, MUSK, AGRN, or LRP4 is currently recruiting.

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Diseases / indications

• Congenital Myasthenic Syndrome

Snippet

Sponsor: argenx | Conditions: Congenital Myasthenic Syndrome | Status: RECRUITING