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CLINICAL_TRIALS research · 2026-03-13

Clinical Trial Update: A Study to Evaluate Long-Term Safety, Tolerability, & Efficacy of BMN 111 in Children With Achondroplasia (ACH) [Phase 2]

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Summary

Phase 2 trial update for BMN 111 (vosoritide) evaluating long-term safety, tolerability, and efficacy in children with achondroplasia. The study is currently ac…

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Diseases / indications

Drugs mentioned

  • Vosoritide (vosoritide)

Snippet

Sponsor: BioMarin Pharmaceutical | Conditions: Achondroplasia | Phase 2 | Status: ACTIVE_NOT_RECRUITING