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CLINICAL_TRIALS research · 2026-03-13

Clinical Trial Update: Gene Therapy for Alpha 1- Antitrypsin Deficiency [Phase 1]

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Summary

Phase 1 clinical trial evaluating a gene therapy for Alpha-1 antitrypsin deficiency, currently recruiting.

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Diseases / indications

Snippet

Sponsor: Weill Medical College of Cornell University | Conditions: Alpha 1-Antitrypsin Deficiency | Phase 1 | Status: RECRUITING