CLINICAL_TRIALS
research
· 2026-03-13
Clinical Trial Update: Gene Therapy for Alpha 1- Antitrypsin Deficiency [Phase 1]
Summary
Phase 1 clinical trial evaluating a gene therapy for Alpha-1 antitrypsin deficiency, currently recruiting.
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Diseases / indications
Snippet
Sponsor: Weill Medical College of Cornell University | Conditions: Alpha 1-Antitrypsin Deficiency | Phase 1 | Status: RECRUITING