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CLINICAL_TRIALS trial_result · 2026-03-13

Clinical Trial Update: An Extension Study to Evaluate Safety and Efficacy of BMN 111 in Children With Achondroplasia [Phase 2]

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Summary

An extension Phase 2 trial is evaluating the safety and efficacy of BMN 111 (vosoritide) in children with Achondroplasia; the study is currently ACTIVE_NOT_RECR…

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Diseases / indications

Drugs mentioned

  • BMN-111 (vosoritide)

Snippet

Sponsor: BioMarin Pharmaceutical | Conditions: Achondroplasia | Phase 2 | Status: ACTIVE_NOT_RECRUITING