CLINICAL_TRIALS
trial_result
· 2026-03-16
Clinical Trial Update: A Safety and Efficacy Study of Cryopreserved OTL-200 for Treatment of Metachromatic Leukodystrophy (MLD) [Phase 2]
Summary
A Phase 2 clinical trial evaluating the safety and efficacy of cryopreserved OTL-200 for Metachromatic Leukodystrophy has completed.
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Diseases / indications
Drugs mentioned
Snippet
Sponsor: Orchard Therapeutics | Conditions: Lysosomal Storage Disease, Metachromatic Leukodystrophy | Phase 2 | Status: COMPLETED