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CLINICAL_TRIALS trial_result · 2026-03-16

Clinical Trial Update: A Safety and Efficacy Study of Cryopreserved OTL-200 for Treatment of Metachromatic Leukodystrophy (MLD) [Phase 2]

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Summary

A Phase 2 clinical trial evaluating the safety and efficacy of cryopreserved OTL-200 for Metachromatic Leukodystrophy has completed.

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Diseases / indications

Drugs mentioned

  • OTL-200

Snippet

Sponsor: Orchard Therapeutics | Conditions: Lysosomal Storage Disease, Metachromatic Leukodystrophy | Phase 2 | Status: COMPLETED