Catalyst Wire Dossier Catalyst Wire Dossier
CLINICAL_TRIALS research · 2026-03-17

Clinical Trial Update: A Study of Pitolisant in Patients With Prader-Willi Syndrome [Phase 3]

View source ↗

Summary

Harmony Biosciences is conducting a Phase 3 trial to evaluate pitolisant for Prader-Willi Syndrome, and recruitment is ongoing.

Upgrade for the full analysis, importance score, and drug timeline.

Diseases / indications

Drugs mentioned

  • Pitolisant (pitolisant)

Snippet

Sponsor: Harmony Biosciences Management, Inc. | Conditions: Prader-Willi Syndrome | Phase 3 | Status: RECRUITING