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CLINICAL_TRIALS research · 2026-03-17

Clinical Trial Update: Study to Evaluate Sepofarsen in Subjects With Leber Congenital Amaurosis (LCA) Type 10 (HYPERION) [Phase 3]

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Summary

The document describes an ongoing Phase 3 clinical trial evaluating Sepofarsen for Leber congenital amaurosis (LCA) type 10, which is currently recruiting.

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Diseases / indications

Drugs mentioned

  • Sepofarsen (sepofarsen)

Snippet

Sponsor: Laboratoires Thea | Conditions: Leber Congenital Amaurosis 10, Blindness | Phase 3 | Status: RECRUITING