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CLINICAL_TRIALS research · 2026-03-17

Clinical Trial Update: A Study of Pitolisant in Participants With Prader-Willi Syndrome [Phase 3]

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Summary

Phase 3 clinical trial evaluating pitolisant for Prader-Willi syndrome is currently enrolling by invitation.

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Diseases / indications

Drugs mentioned

  • Pitolisant (pitolisant)

Snippet

Sponsor: Harmony Biosciences Management, Inc. | Conditions: Prader-Willi Syndrome | Phase 3 | Status: ENROLLING_BY_INVITATION