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CLINICAL_TRIALS research · 2026-03-18

Clinical Trial Update: A Study in Adult Patients With Paroxysmal Nocturnal Hemoglobinuria (PNH) to Evaluate How Safe Long-term Treatment With Pozelimab + Cemdisiran Combination Therapy is and How Well it Works [Phase 3]

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Summary

Phase 3 study evaluating long-term safety and efficacy of Pozelimab plus Cemdisiran in adults with paroxysmal nocturnal hemoglobinuria; recruitment is ongoing.

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Diseases / indications

Drugs mentioned

  • Cemdisiran (cemdisiran)
  • Pozelimab

Snippet

Sponsor: Regeneron Pharmaceuticals | Conditions: Paroxysmal Nocturnal Hemoglobinuria | Phase 3 | Status: RECRUITING