CLINICAL_TRIALS
research
· 2026-03-18
Clinical Trial Update: A Study in Adult Patients With Paroxysmal Nocturnal Hemoglobinuria (PNH) to Evaluate How Safe Long-term Treatment With Pozelimab + Cemdisiran Combination Therapy is and How Well it Works [Phase 3]
Summary
Phase 3 study evaluating long-term safety and efficacy of Pozelimab plus Cemdisiran in adults with paroxysmal nocturnal hemoglobinuria; recruitment is ongoing.
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Diseases / indications
Drugs mentioned
Snippet
Sponsor: Regeneron Pharmaceuticals | Conditions: Paroxysmal Nocturnal Hemoglobinuria | Phase 3 | Status: RECRUITING