Clinical Trial Update: A Study to Evaluate the Safety and Efficacy of Nizubaglustat (AZ-3102) in Patients With GM2 Gangliosidosis or Niemann-Pick Type C Disease [Phase 2]

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Summary

A Phase 2 clinical trial is evaluating the safety and efficacy of Nizubaglustat (AZ-3102) in patients with GM2 gangliosidosis and Niemann-Pick disease type C, c…

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Diseases / indications

• Gm2 Gangliosidosis
• Niemann-pick Disease Type

Drugs mentioned

• Nizubaglustat

Snippet

Sponsor: Azafaros A.G. | Conditions: GM2 Gangliosidosis, Niemann-Pick Type C Disease | Phase 2 | Status: RECRUITING