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CLINICAL_TRIALS research · 2026-03-23

Clinical Trial Update: Natural History Study for Patients With Nemaline Myopathy in Spain

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Summary

Clinical trial update for a natural history study of Nemaline Myopathy in Spain; currently recruiting to document disease progression and natural history.

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Diseases / indications

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Sponsor: Hospital Universitari Vall d'Hebron Research Institute | Conditions: Nemaline Myopathy, Myopathies | Status: RECRUITING